Advances in Therapeutic Development Across Modalities

Symposium: Recent Advances in Gene Therapy

Moderator(s)

• 

  Catherine Vrentas, PhD

  Senior Research Scientist
  PPD, A ThermoFisher Company
  Richmond, United States

Presentations:

• 9:30 AM – 10:00 AM ET

  Immunogenicity Assessment and Mitigation of AAV-Based Gene Therapies
  

  Speaker: Tong-Yuan Yang, PhD (he/him/his) – Janssen Research & Development, LLC
• 10:00 AM – 10:30 AM ET

  Translational and Dosing Considerations for Ocular AAV-Based Gene Therapy
  

  Speaker: Prathap Nagaraja Shastri, PhD – Johnson and Johnson
• 10:30 AM – 11:00 AM ET

  Biomarker and Bioanalytical Data from imagine-1:assessing PBGM01 for GM1 Gangliosidosis
  

  Speaker: Yan G. Ni, PhD – Passage Bio