SSC 13 - SSC Session - Factor VIII, Factor IX and Rare Coagulation Disorders

Presentations:

• 4:30 PM – 4:34 PM

  Welcome and Introduction
  

  Speaker: Johnny Mahlangu, MD, MMed – University of the Witwatersrand and NHLS
• 4:34 PM – 4:44 PM

  Low Dose Prophylaxis With Emicizumab: A Dream or Reality?
  

  Speaker: Kathelijn Fischer, MD, PhD – Center for Benign Haematology, Thrombosis and Haemostasis, Van Creveldkliniek, University Medical Center Utrecht, Utrecht University, The Netherlands
• 4:44 PM – 4:54 PM

  New Non-replacement Therapies: Is biv001 the Answer We Are All Looking For?
  

  Speaker: Barbara A. Konkle, MD – University of Washington
• 4:54 PM – 5:04 PM

  Development of Novel Proteins With Enhanced Activity for Bleeding Disorders
  

  Speaker: Benjamin J. Samelson-Jones, PhD – Division of Hematology and the Raymond G. Perelman Center for Cellular and Molecular Therapeutics, Children’s Hospital of Philadelphia
• 5:04 PM – 5:14 PM

  Gene Therapy for Inhibitor Patients: What Is the Rationale?
  

  Speaker: David A. Wilcox, PhD – Medical College of Wisconsin
• 5:14 PM – 5:24 PM

  Is the Development of Cancer an Issue in Hemophilia Gene Therapy?
  

  Speaker: Margareth C. Ozelo, MD, PhD – University of Campinas, UNICAMP
• 5:24 PM – 5:34 PM

  Q&A
  

  Speaker: Sabine Heine, MD – Universitätskinderklinik des Saarlandes

  Speaker: Miguel Escobar, MD – University of Texas Health Science Center of Houston, McGovern Medical School, Gulf States Hemophilia and Thrombophilia Center, Houston, Texas
• 5:34 PM – 5:44 PM

  What Are the Standardization Issues in the Diagnosis of Rare Bleeding Disorders?
  

  Speaker: Tarek Owaidah, MD – alfaisal university
• 5:44 PM – 5:54 PM

  Novel Therapeutic Strategies for Alloimmunization in Glanzmann Thrombasthaenia
  

  Speaker: Vijay Bhoj, MD, PhD – University of Pennsylvania
• 5:54 PM – 6:04 PM

  Value Assignment to the WHO 9th International Standard for Factor VIII Concentrate: Collaborative Study Update
  

  Speaker: Sanj Raut, PhD – NIBSC-MHRA
• 6:04 PM – 6:14 PM

  The Influence of von Willebrand Factor on Factor VIII Activity Measurements
  

  Speaker: Cornelis Kluft, PhD – Good Biomarker Sciences
• 6:14 PM – 6:24 PM

  PUP nomenclature working group
  

  Speaker: Guy Young, MD – Children's Hospital Los Angeles
• 6:24 PM – 6:30 PM

  Q&A
  

  Speaker: Savita Rangarajan, MD, FRCP, FRCPath – Faculty of Medicine, University of Southampton, Southampton, UK

  Speaker: John Pasi, MB ChB PhD – Queen Mary University of London / Roche Products Ltd