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Developing an Innovative CNS Targeted Therapy for Aicardi-Goutières Syndrome

Friday, June 24, 2022

3:20 PM – 3:45 PM PT

Location: Salons 1/2

Speaker(s)

Terry Fang, PhD

Director
Biogen
Newton, Massachusetts, United States

PDF

Chair(s)

Terri Laufer, MD

Associate Professor of Medicine
University of Pennsylvania
Philadelphia, Pennsylvania, United States

Learning Objectives:

Describe clinical features of Aicardi-Goutieres Syndrome
Understand the molecular basis for anti-sense oligonucleotide therapy
Describe approaches to development of CNS fluid biomarkers